Research LetterIn-Press PreviewGastroenterologyGeneticsNeuroscience
Open Access | 
10.1172/jci.insight.202780
Characterizing enteric pathology in MPS IIIA mice suggests disease-specific vulnerability among lysosomal storage disorders
Ewa A. Ziółkowska,1 Letitia L. Williams,1 Elizabeth M. Eultgen,1 Grace R. Kick,1 Xukai Ding,1 Alexander Sorensen,1 Steven Q. Le,1 Balraj Doray,1 Patricia I. Dickson,1 Robert O. Heuckeroth,2 and Jonathan D. Cooper1
1Departments of Pediatrics, Washington University in St. Louis, St. Louis, United States of America
2Children’s Hospital of Philadelphia Research Institute, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, United States of America
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1Departments of Pediatrics, Washington University in St. Louis, St. Louis, United States of America
2Children’s Hospital of Philadelphia Research Institute, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, United States of America
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1Departments of Pediatrics, Washington University in St. Louis, St. Louis, United States of America
2Children’s Hospital of Philadelphia Research Institute, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, United States of America
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1Departments of Pediatrics, Washington University in St. Louis, St. Louis, United States of America
2Children’s Hospital of Philadelphia Research Institute, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, United States of America
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1Departments of Pediatrics, Washington University in St. Louis, St. Louis, United States of America
2Children’s Hospital of Philadelphia Research Institute, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, United States of America
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1Departments of Pediatrics, Washington University in St. Louis, St. Louis, United States of America
2Children’s Hospital of Philadelphia Research Institute, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, United States of America
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1Departments of Pediatrics, Washington University in St. Louis, St. Louis, United States of America
2Children’s Hospital of Philadelphia Research Institute, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, United States of America
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1Departments of Pediatrics, Washington University in St. Louis, St. Louis, United States of America
2Children’s Hospital of Philadelphia Research Institute, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, United States of America
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1Departments of Pediatrics, Washington University in St. Louis, St. Louis, United States of America
2Children’s Hospital of Philadelphia Research Institute, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, United States of America
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1Departments of Pediatrics, Washington University in St. Louis, St. Louis, United States of America
2Children’s Hospital of Philadelphia Research Institute, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, United States of America
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1Departments of Pediatrics, Washington University in St. Louis, St. Louis, United States of America
2Children’s Hospital of Philadelphia Research Institute, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, United States of America
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Cooper, J.
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Published July 23, 2026 - More info
Copyright © 2026, Ziółkowska et al. This work is licensed under the Creative Commons Attribution 4.0 International License. To view a copy of this license, visit http://creativecommons.org/licenses/by/4.0/.
