Zoheb B. Kazi, Sean N. Prater, Joyce A. Kobori, David Viskochil, Carrie Bailey, Renuka Gera, David W. Stockton, Paul McIntosh, Amy S. Rosenberg, Priya S. Kishnani
Dosing profile of recombinant human acid alpha-glucosidase (rhGAA) and immunomodulation, as well as rhGAA IgG antibody titers, left ventricular mass index (A and B; in g/m2), and urinary glucose tetrasaccharide (in mmol/mol creatinine) over time for Patient 1.
Glc4, glucose tetrasaccharide; LVMI, left ventricular mass index; ERT, enzyme replacement therapy; IVIG, i.v. immunoglobulin. Upper limit of normal LVMI is 64 g/m2 (