A functional scale for spinal and bulbar muscular atrophy: cross-sectional and longitudinal study
A Hashizume, M Katsuno, K Suzuki, H Banno… - Neuromuscular …, 2015 - Elsevier
We aimed to develop, validate, and evaluate a disease-specific outcome measure for SBMA:
the Spinal and Bulbar Muscular Atrophy Functional Rating Scale (SBMAFRS). We examined
the Japanese version (SBMAFRS-J) in 80 Japanese SBMA subjects to evaluate its validity
and reliability. We then assessed this scale longitudinally in 41 additional SBMA subjects.
The English version (SBMAFRS-E) was also tested in 15 US subjects. The total score of the
SBMAFRS-J was distributed normally without an extreme ceiling or floor effect. For …
the Spinal and Bulbar Muscular Atrophy Functional Rating Scale (SBMAFRS). We examined
the Japanese version (SBMAFRS-J) in 80 Japanese SBMA subjects to evaluate its validity
and reliability. We then assessed this scale longitudinally in 41 additional SBMA subjects.
The English version (SBMAFRS-E) was also tested in 15 US subjects. The total score of the
SBMAFRS-J was distributed normally without an extreme ceiling or floor effect. For …