Zoheb B. Kazi, Sean N. Prater, Joyce A. Kobori, David Viskochil, Carrie Bailey, Renuka Gera, David W. Stockton, Paul McIntosh, Amy S. Rosenberg, Priya S. Kishnani
Key laboratory findings at enzyme replacement therapy start, bortezomib start, and at most recent follow-up at time of database lock for the 3 patients with infantile Pompe disease.A